Market Research Reports, Inc. has announced the addition of “Global Pompe Disease Treatment Market 2016 - 2020” research report to their offering. See more at - http://mrr.cm/3RP

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Category : Healthcare
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Introduction to Report
 Launch Date: December 13, 2016
 Number of Pages: 65
 Geography Coverage: Global
 Available Format: PDF
Price For Single User License: USD 2,500
Price For Site User License: USD 4,000
Price For Global User License: USD 10,000
Delivery Time: Within 24 Hours (During Working
Days)

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About the Report
Global Pompe Disease Treatment Market 2016-
2020, has been prepared based on an in-depth
market analysis with inputs from industry experts.
The report covers the market landscape and its
growth prospects over the coming years. The
report also includes a discussion of the key
vendors operating in this market.
Report forecast the global Pompe disease
treatment market to grow at a CAGR of 11.85%
during the period 2016-2020.

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Key Highlights:
Lysosomal storage diseases (LSDs) are a group of
progressive, autosomal recessive, and hereditary
disorders characterized by the accumulation of specific
substrates and variable age of onset and clinical
symptoms.
Pompe disease, a type of LSD, is caused by mutations
in the GAA gene.
These mutations inhibit the mechanism of action
(MOA) of GAA; it is an enzyme responsible for
catabolizing glycogen, resulting in accumulation of
glycogen to toxic levels in the lysosomes of the cells.
The buildup of glycogen in certain tissues and organs,
especially in the muscles, hinders the normal functions
of the organs.
It can be further divided as adult-onset and infantile-
onset Pompe diseases.

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Key Highlights: Continues…
As the disease is an autosomal recessive hereditary
disorder, both parents are carriers and pass one copy of
the mutated gene to their offspring.
The report covers the present scenario and the growth
prospects of the global Pompe disease treatment
market for 2016-2020.
To calculate the market size, the report considers the
revenue generated from the sales of the drugs available
in the market and the drug candidates that are in
various phases of development for the treatment of
Pompe disease.

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Key Questions Answered in this Report
What will the market size be in 2020 and what will
the growth rate be?
What are the key market trends?
What is driving this market?
What are the challenges to market growth?
Who are the key vendors in this market space?
What are the market opportunities and threats
faced by the key vendors?
What are the strengths and weaknesses of the
key vendors?

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Report Coverage:
1. Executive summary
2. Scope of the report
3. Market research methodology
4. Introduction
5. Disease overview
6. Market landscape
7. Geographical segmentation
8. Market drivers
9. Impact of drivers
10. Market challenges
11. Impact of drivers and challenges
For more details regarding Report coverage see the last slide
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Report Coverage: Continues…
12. Market segmentation by type of Pompe
disease
13. Market trends
14. Vendor landscape
15. Key vendor analysis
16. Appendix
For more details regarding Report coverage see the last slide
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Company Coverage:
1. Amicus Therapeutics
2. Audentes Therapeutics
3. Sanofi-Genzyme
4. EpiVax
5. Oxyrane
6. Sangamo BioSciences
7. Valerion Therapeutics
For more details regarding Report coverage see the last slide
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How To Buy This Report?
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About Market Research Reports, Inc.
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